How genetics shape blood proteins during development from childhood to adolescence
Blood proteins serve as crucial indicators of health and disease risk throughout development. Now, researchers at the ...
Researchers investigate rare side effect of blood cancer immunotherapy
Researchers have discovered and analyzed a rare but serious side effect of an innovative form of blood cancer therapy. The ...
Healio3h
FDA approves first treatment for rare lipid storage disease
The FDA has approved Ctexli for the treatment of cerebrotendinous xanthomatosis (CTX), a rare lipid storage disease, in ...
Combined organ-specific mRNA and lipid nanoparticle therapy could repair damaged lungs
A combination of mRNA and a new lipid nanoparticle could help heal damaged lungs, according to new research from the Perelman ...
Healio15h
BLOG: Optimizing donor selection in aplastic anemia — evolving trends in transplantation
Aplastic anemia is a bone marrow failure process that presents with pancytopenia and bone marrow hypoplasia/aplasia.It ...
Cure Today11h
Tuspetinib Triplet Is Safe and Has Antileukemic Activity in Newly Diagnosed AML
Treatment with tuspetinib in combination with Venclexta and Vidaza in newly diagnosed acute myeloid leukemia showed safety ...
ENDPOINTS NEWS4h
FDA ap­proves first drug to treat ul­tra-rare lipid stor­age dis­ease
The FDA on Friday approved Mirum Pharmaceuticals' Ctexli to treat adults with cerebrotendinous xanthomatosis (CTX), a rare, progressive and genetic disease.