Anderson’s push in the pediatric rare disease space remains driven by the 2019 loss of his son Andrew to Tay-Sachs disease. “That’s my favorite part of working in this field, getting to know ...
Jacksonville Journal-Courier on MSN2d
SamJam fundraiser back for one last goOne of the most popular music festivals in small-town Illinois is coming to an end after a 10-year run. SamJam’s Finale is ...
Rare diseases - a medical condition so obscure that even your doctor has to Google. Despite their name, these diseases ...
One childless man’s journey through the sci-fi start-ups, DIY donor clubs, and group masturbation retreats attempting to save ...
More patient-centric study design, using mHealth for longer-term monitoring, will address many of the inherent challenges in conducting pivotal clinical trials in rare diseases, argues Elin Haf ...
Children born with Tay-Sachs disease, for instance, lack a critical enzyme necessary for the body to metabolize a fatty waste substance found in the brain. The disease is very rare and occurs only ...
The issue of rare diseases is one Anderson often champions. His son, Andrew, suffered from Tay-Sachs disease, an ultrarare fatal genetic disorder with only 16 cases annually nationwide.
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