Meet the La Jolla researcher who helped discover new muscular dystrophy drug
Having found that in biomedical research, the Bird Rock resident and scientist at La Jolla’s Sanford Burnham Prebys has ...
Daily Post Nigeria on MSN1d
Kano Assembly passes bills to create Deputy MD positions in key agencies
The Kano State House of Assembly has passed five amended bills aimed at creating the office of a Deputy Managing Director ...
'He talked about dying... how do you even answer that?'
The mum of an 11-year-old boy who is waiting to find out if he can access a new drug to treat his Duchenne muscular dystrophy ...
Independent.ie on MSN2h
Kerry staff come together to help seven-year old Archie get treatment
Seven-year-old Archie Ennis has touched the hearts of the nation as his family plea for funds to help him get the life-saving ...
The American Journal of Managed Care13d
Survey Explores Needs of Patients With DMD, BMD Transitioning to Adulthood
Activities of daily life, education, and employment were areas of difficulty in the transition to adulthood for patients with ...
The Cardiology Advisor3d
Deramiocel Granted Priority Review for DMD Cardiomyopathy
The FDA has granted Priority Review to the BLA for deramiocel (CAP-1002) for the treatment of Duchenne muscular dystrophy cardiomyopathy.
Fierce Biotech9d
PepGen pauses UK arm of DMD trial that's already on hold in US
While PepGen works to persuade the FDA to let it launch a phase 2 trial of its Duchenne muscular dystrophy (DMD) therapy in ...
PepGen Announces Update to Phase 2 CONNECT2-EDO51 Study in Patients with DMD
PepGen Inc. (Nasdaq: PEPG), a clinical-stage biotechnology company advancing the next generation of oligonucleotide therapies ...
Sarepta Therapeutics' Long-Term Potential Intact Despite Near-Term Stock Weakness
Sarepta Therapeutics hits 52-week lows despite strong earnings and growth. Read why investors should view SRPT as a high risk ...
GlobalData on MSN9d
CureDuchenne, CHOC partner to establish clinic for DMD patients
US-based CureDuchenne has formed a partnership with Children's Hospital of Orange County (CHOC) to launch a new clinic for ...
Capricor: Further Value Unlocked With Priority Review Of Deramiocel
Capricor Therapeutics, Inc.'s Deramiocel receives FDA Priority Review for DMD cardiomyopathy, with a decision by Aug. 2025.
Monthly Prescribing Reference10d
Deramiocel Granted Priority Review for DMD Cardiomyopathy
In male patients with DMD, treatment with deramiocel reduced upper limb function deterioration compared with placebo. The Food and Drug Administration (FDA) has granted Priority Review to the ...